Just In
- 38 min ago Daily Horoscope, 29 March 2024: Gemini Businessmen Should Be Careful, Leo May Not Feel Well Today
- 5 hrs ago Aditi Rao Hydari's 8 Tips for Glowing Skin: A Celebrity Skincare Routine Unveiled, Bonus Tips Included!
- 5 hrs ago April 2024 Health Horoscope: Know How This Month Will Affect Zodiac Signs In Terms Of Wellness
- 6 hrs ago Good Friday 2024: Wishes, Messages, Greetings, Texts, Images, Quotes, WhatsApp, And FB Status
Don't Miss
- Movies Panchayat 3 Release Date: When Will Jitendra Kumar's Web Series Release On OTT? Latest Update
- Finance 1:5 Stock Split Charm: From Rs 650-To-8,800, Midcap Stock To Explode Further, Target Highest At Rs 10,950
- Sports Rajasthan Royals Rising Star Riyan Parag's Redemption Story Takes Center Stage in IPL 2024
- News Jailed Gangster-Turned-Politician Mukhtar Ansari Dies Of Heart Attack
- Automobiles Xiaomi SU7 Electric Car Launched – May End Apple Inc.
- Technology HONOR Pad 9 With Bluetooth Keyboard Up For Grabs At Rs 22,499 in India
- Education RSMSSB Junior Instructor Recruitment 2024; Apply online for 2500 Posts, Check out for more details
- Travel Explore Tamil Nadu's Diverse Wedding Venues
FDA Approves Most Expensive Drug Ever, Priced At $3.5 Million-Per-Dose For Hemophilia
A $3.5 million (₹285,320,350.00 INR) one-time treatment for hemophilia has been approved by U.S. FDA on Tuesday. For adults with hemophilia B, a less common form of the genetic disorder which primarily affects men, the Food and Drug Administration has approved Hemgenix, an IV treatment for the disease [1].
Details About The Most Expensive Drug Ever
"Today's approval provides a new treatment option for patients with hemophilia B and represents important progress in the development of innovative therapies," said the FDA's Dr. Peter Marks [2].
Point 1: Hemgenix is the most expensive medicine in the world according to a study cited by the National Library of Medicine, easily topping Novartis' Zolgensma gene therapy for spinal muscular atrophy (SMA), which costs just over $2 million (163,310,022 INR per dose) and is also a single-dose treatment [3].
Point 2: According to the agency, patients should benefit from the treatment for years to come due to reduced bleeding and increased clotting.
Point 3: The Pennsylvania-based drugmaker CSL Behring announced the price tag shortly after FDA approval, claiming the drug would ultimately reduce health care costs by reducing bleeding incidents and clotting treatments.
Point 4: Most of the costs of the new treatment will be covered by insurers, not patients, including private plans and government programs [4].
What Is Haemophilia?
A person with haemophilia usually has an inherited bleeding disorder that can cause spontaneous bleeding as well as bleeding following an injury or surgical procedure. The blood contains several proteins called clotting factors that can prevent bleeding [5].
The two most common types of haemophilia are Haemophilia A (Classic Haemophilia), caused by a lack of or decrease in clotting factor VIII, and Haemophilia B (Christmas Disease), caused by a lack or decrease in clotting factor IX.
One in every 5,000 males is born with haemophilia A, which is four times as common as haemophilia B, and about half of those with haemophilia A are affected by the severe form [6].
It is rare for someone to develop haemophilia at a later stage in life. In this case, hemophilia tends to affect people in their middle age or elderly, as well as young women who have recently given birth or are in the later stages of pregnancy. Treatment is usually effective in resolving this condition.
When left untreated, haemophilia can cause bleeding that seeps into joints and internal organs, including the brain. Small cuts and bruises can cause life-threatening bleeding for people with haemophilia.
The prevalence of haemophilia in India is low, at 0.7 per 1,000 people.
- wellnessThe FDA Approved A New Drug Aduhelm To Treat Alzheimer’s, But Medicare Insurance Won’t Always Pay For It
- disorders cureCOVID-19: FDA Authorizes Blood Purification Device For Treatment Of Coronavirus
- disorders cureDrug For Anemic Cancer May Raise Death Risk!
- healthWorld HIV/AIDS Day: Ancient AIDS Treatments: Did They Stand the Test of Time?
- beautyWhen Is It Time To Get Medical Treatment For Acne And Pimples?
- healthCan You Get Back COVID-Related Loss Of Sense Of Smell And Taste (Parosmia)? Looks Like You Can!
- healthWorld Pancreatic Cancer Day 2023: Date, Theme, Significance & Everything About It
- healthWorld Diabetes Day 2023: 3 Weird Things That Can Put You At Risk Of Developing Diabetes
- healthCancer: Scalp-Cooling Technology May Help Some Chemo Patients Keep Their Hair
- healthWhat Is The Right Age To Get Breast Cancer Screening?
- wellnessTry These 5 Hot Beverages For Relief From Common Cold
- wellness4 Best Home Remedies For Body Pain Caused By Dengue Fever